Lecture

Personalized Medicine: Gene Therapy and CRISPR

Related lectures (32)

Explores gene therapy targets, RNA-based therapeutics, and recent advancements in genetic treatments for monogenic diseases and cancer.

Choosing a Viral Vector and Delivery Method

Discusses viral vector selection for gene therapy, with a focus on AAV vectors for SMA1 therapy and CNS delivery.

Non Viral Vectors

Explores the use of non-viral vectors for precise nucleic acid delivery and their limitations in achieving long-term gene expression.

Gene Therapy: RNA Therapeutics & Monogenic Diseases

Explores gene therapy, RNA therapeutics, monogenic diseases, CAR T cell therapy, and CRISPR-based treatments.

Personalized Medicine: The Future of Healthcare

Delves into personalized medicine, showcasing recent technological advances and challenges in healthcare.

Types of Viral Vectors

Explores the properties of commonly used viral vectors for gene therapy.

Synthetic Biology: Engineering Living Systems

Explores synthetic biology, emphasizing protein engineering, gene circuits, and cellular design for diverse applications.

Genetic Toggle Switch: Synthetic Biology Example

Covers the construction of a genetic toggle switch in Escherichia coli, a key example of synthetic biology.

B-Cell Receptor Signaling in Lymphoma and Leukemia

Explores B-cell receptor signaling in lymphoma and leukemia, drug resistance mechanisms, CRISPR/Cas9 gene editing, mTOR inhibitors, cell cycle inhibition, and undruggable oncogenes.

Immune Cell Engineering: Targeting Checkpoint Inhibitors

Explores immune cell engineering for cancer therapy, emphasizing checkpoint inhibitor targeting through innovative delivery methods.

DNA: PCR and Sequencing Techniques

Explores DNA engineering through PCR, Sanger sequencing, the Human Genome Project, recombinant DNA, bacterial DNA manipulation, and CRISPR/Cas9.

Metabolic Engineering: Tools and Concepts

Explores metabolic engineering tools, synthetic biology objectives, and metabolic pathway analysis for understanding cell physiology.