Mediaspace scheduled maintenance: Aug 25, 2026 07:00 - 12:00 AM. During this time, videos will be temporarily unavailable. Check status updates.

Concept

Gene therapy of the human retina

Related lectures (32)

Production of Viral Vectors MOOC: Neuroscience Reconstructed: Genetics and Brain Development

Explores the production of viral vectors for gene therapy applications, emphasizing AAV vectors and the process of large-scale production and purification.

AAV Vectors: Development and Applications MOOC: Neuroscience Reconstructed: Genetics and Brain Development

Explores the development and applications of AAV vectors, highlighting their specificity and stability for gene therapy.

Types of Viral Vectors MOOC: Neuroscience Reconstructed: Genetics and Brain Development

Explores the properties of commonly used viral vectors for gene therapy.

Non Viral Vectors MOOC: Neuroscience Reconstructed: Genetics and Brain Development

Explores the use of non-viral vectors for precise nucleic acid delivery and their limitations in achieving long-term gene expression.

Preclinical and Clinical Trials in SMA Gene Therapy MOOC: Neuroscience Reconstructed: Genetics and Brain Development

Explores preclinical and clinical trials in SMA gene therapy, including efficiency in patients, trial results, adverse effects, cellular targeting, and future perspectives.

Choosing a Viral Vector and Delivery Method MOOC: Neuroscience Reconstructed: Genetics and Brain Development

Discusses viral vector selection for gene therapy, with a focus on AAV vectors for SMA1 therapy and CNS delivery.

Human Visual System

Covers the study of the Human Visual System, including anatomy, color perception, retina processing, and focus of attention models.

Receptive Field Development

Explores receptive fields in neurobiology, from basic concepts to complex formations and neural plasticity.

Visual Prostheses: History and Intracortical Stimulation

Explores the history and challenges of visual prostheses, focusing on intracortical microstimulation for artificial vision.

Optical Coherence Tomography: Techniques and Applications

Covers the principles and applications of Optical Coherence Tomography in various fields, including medical diagnostics and materials science.

Gene Therapy for CNS and Sensory Organs

Explores gene therapy for CNS and sensory organs, focusing on rare genetic diseases and advancements in precision medicine.

Personalized Medicine: The Future of Healthcare

Delves into personalized medicine, showcasing recent technological advances and challenges in healthcare.

Gene Therapy: RNA Therapeutics & Monogenic Diseases

Explores gene therapy, RNA therapeutics, monogenic diseases, CAR T cell therapy, and CRISPR-based treatments.

Drug Targets: Receptors, Enzymes, and Transporters

Explores drug targets like receptors, enzymes, and transporters, focusing on top drug indications and receptor-mediated activation of G proteins.

Visual Information Processing: Eye and Implants

Covers the processing of visual information in the eye, the anatomy of the retina, the biochemistry of photoreceptors, and the use of implants to treat visual impairments.

Approaches in Gene Therapy MOOC: Neuroscience Reconstructed: Genetics and Brain Development

Discusses approaches in gene therapy for different diseases and the advantages of gene transfer over conventional drugs, as well as viral vectors for gene delivery.

Gene Therapy: Targets and Therapeutics

Explores gene therapy targets, RNA-based therapeutics, and recent advancements in genetic treatments for monogenic diseases and cancer.

Personalized Medicine: Gene Therapy and CRISPR

Explores personalized medicine, gene therapy, CRISPR technology, gene editing strategies, and ethical implications of synthetic genomics.

Opponency Revisited

Explores the concept of opponency in color vision, covering trichromatic color vision, opponent colors, and receptive fields.

Protein Life Cycle

Covers gene expression, protein life cycle, and genetic code in neuroscience.